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Reversal of malignant ADAR1 splice isoform switching with Rebecsinib
Affiliation:1. Department of Medicine, Division of Regenerative Medicine, Sanford Stem Cell Institute, University of California, San Diego, La Jolla, CA 92037, USA;2. Moores Cancer Center, University of California, San Diego, La Jolla, CA 92093, USA;3. Center for Computational Biology & Bioinformatics (CCBB), Department of Medicine, University of California, San Diego, La Jolla, CA 92093, USA;4. Departments of Chemistry and Biochemistry, University of California, San Diego, La Jolla, CA 92093, USA
Abstract:
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  • Keywords:myeloproliferative neoplasms  myelofibrosis  secondary AML  leukemia stem cells  splicing  RNA editing  ADAR1  hematopoiesis  cancer stem cells  cancer therapy
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