Gene Therapy for LMNA-related Congenital Muscular Dystrophy (L-CMD) by Trans-Splicing |
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Authors: | Feriel Azibani Anne T Bertrand |
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Affiliation: | 1.Sorbonne Universités, UPMC Univ Paris 06, INSERM UMRS974, CNRS FRE3617, Center for Research in Myology,Paris,France |
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