Institution: | 1.San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan 20132, Italy;2.Translational and Molecular Medicine (DIMET), University of Milano-Bicocca, Monza 20900, Italy;3.Institute of Genetic and Biomedical Research, Milan Unit, National Research Council, Milan 20090, Italy |