Affiliation: | 1. Stem Cell Transplantation Program;2. Division of Pediatric Hematology/Oncology;3. Manton Center for Orphan Disease Research;4. Howard Hughes Medical Institute;5. Children's Hospital Boston and Dana Farber Cancer Institute;6. Division of Hematology;7. Brigham and Women's Hospital;8. Boston, MA USA;9. Department of Biological Chemistry and Molecular Pharmacology;10. Harvard Medical School;11. Harvard Stem Cell Institute;12. Howard Hughes Medical Institute;13. Department of Biomedical Engineering and Center of Synthetic Biology;14. Boston University;15. Wyss Institute for Biologically Inspired Engineering;16. Harvard University |