Affiliation: | 1.Stem Cell Transplantation Program, Division of Pediatric Hematology/Oncology, Manton Center for Orphan Disease Research, Howard Hughes Medical Institute, Children''s Hospital Boston and Dana Farber Cancer Institute, Boston, MA 02115, USA;2.Department of Biological Chemistry and Molecular Pharmacology, Harvard Medical School, Boston, MA 02115, USA;3.Broad Institute, Boston, MA 02115, USA;4.Harvard Stem Cell Institute, Boston, MA 02115, USA |