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Counteracting chromatin effects of a splicing-correcting antisense oligonucleotide improves its therapeutic efficacy in spinal muscular atrophy
Affiliation:1. Universidad de Buenos Aires (UBA), Facultad de Ciencias Exactas y Naturales, Departamento de Fisiología, Biología Molecular y Celular and CONICET-UBA, Instituto de Fisiología, Biología Molecular y Neurociencias (IFIBYNE), 1428 Buenos Aires, Argentina;2. Sir William Dunn School of Pathology, University of Oxford, Oxford OX1 3RE, UK;3. Instituto de Medicina Molecular João Lobo Antunes, University of Lisbon, 1649-028 Lisboa, Portugal;4. Cold Spring Harbor Laboratory, Cold Spring Harbor, NY 11724, USA
Abstract:
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