|
|||||
|
|
α‐ l‐iduronidase gene‐based therapy using the phiC31 system to treat mucopolysaccharidose type I mice |
|
| Authors: | Roberta Sessa Stilhano Priscila Keiko Matsumoto Martin Suely Maymone de Melo Vivian Yochiko Samoto Giovani Bravin Peres Yara Maria Correa da Silva Michelacci Flavia Helena da Silva Vanessa Gonçalves Pereira Vania D'Almeida Adriana Taveira da Cruz Miriam Galvonas Jasiulionis Sang Won Han |
| Affiliation: | 1. Department of Biophysics, Universidade Federal de S?o Paulo, S?o Paulo, Brazil;2. Department of Biochemistry, Universidade Federal de S?o Paulo, S?o Paulo, Brazil;3. Department of Pediatrics, Universidade Federal de S?o Paulo, S?o Paulo, Brazil;4. Department of Microbiology, Immunology and Parasitology, Universidade Federal de S?o Paulo, S?o Paulo, Brazil |
| Abstract: | |
| Keywords: | gene therapy IDUA mucopolysaccharidose type I phiC31 integrase |