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Pharmacodynamic Study of Miransertib in Individuals with Proteus Syndrome
Authors:Kim M Keppler-Noreuil  Julie C Sapp  Marjorie J Lindhurst  Thomas N Darling  Jasmine Burton-Akright  Mohammadhadi Bagheri  Eva Dombi  Ashlyn Gruber  Paul F Jarosinski  Staci Martin  Neera Nathan  Scott M Paul  Ronald E Savage  Pamela L Wolters  Brian Schwartz  Brigitte C Widemann  Leslie G Biesecker
Institution:1. Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, NIH, Bethesda, MD 20892, USA;2. Department of Dermatology, Uniformed Services University of Health Sciences, Bethesda, MD 20814, USA;3. Clinical Center Radiology Department, NIH, Bethesda, MD 20892, USA;4. Pediatric Oncology Branch, National Cancer Institute, NIH, Bethesda, MD 20892, USA;5. Pharmacy Department, NIH Clinical Center, NIH, Bethesda, MD 20892, USA;6. Health Psychology and Neurobehavioral Research Group, National Cancer Institute, NIH, Bethesda, MD 20892, USA;7. Physical Medicine Section, NIH Clinical Center, NIH, Bethesda, MD 20892, USA;8. ArQule, Inc., Burlington, MA 01803, USA
Abstract:
Keywords:Proteus syndrome  mosaicism  overgrowth  miransertib  connective tissue nevus  phase I study
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