|
|||||
|
|
Improved Antisense Oligonucleotide Design to Suppress Aberrant SMN2 Gene Transcript Processing: Towards a Treatment for Spinal Muscular Atrophy |
|
| Authors: | Chalermchai Mitrpant Paul Porensky Haiyan Zhou Loren Price Francesco Muntoni Sue Fletcher Steve D. Wilton Arthur H. M. Burghes |
| Abstract: | |
| Keywords: | |