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Novel Adeno‐Associated Viral Vector Delivering the Utrophin Gene Regulator Jazz Counteracts Dystrophic Pathology in mdx Mice
Authors:Georgios Strimpakos  Nicoletta Corbi  Cinzia Pisani  Maria Grazia Di Certo  Annalisa Onori  Siro Luvisetto  Cinzia Severini  Francesca Gabanella  Lucia Monaco  Elisabetta Mattei  Claudio Passananti
Institution:1. Institute of Cell Biology and Neurobiology CNR, IRCCS Fondazione Santa Lucia, Rome, Italy;2. Institute of Molecular Biology and Pathology CNR, Department of Molecular Medicine, Sapienza University, Rome, Italy;3. Department of Physiology and Pharmacology, University Sapienza, Rome, Italy
Abstract:
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