Affiliation: | 1.Dominick P. Purpura Department of Neuroscience, Rose F. Kennedy Intellectual and Developmental Disabilities Research Center, Albert Einstein College of Medicine, Bronx, NY 10461, USA;2.Institute of Inherited Metabolic Disorders, Charles University in Prague –, 1st Faculty of Medicine, Ke Karlovu 2, Praha 2 160 00, Czech Republic |