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Sustained transgene expression by human cord blood derived CD34+ cells transduced with simian immunodeficiency virus agmTYO1-based vectors carrying the human coagulation factor VIII gene in NOD/SCID mice
Authors:Kikuchi Jiro  Mimuro Jun  Ogata Kyoichi  Tabata Toshiaki  Ueda Yasuji  Ishiwata Akira  Kimura Kouzoh  Kimura Konzoh  Takano Katsuhiro  Madoiwa Seiji  Mizukami Hiroaki  Hanazono Yutaka  Kume Akihiro  Hasegawa Mamoru  Ozawa Keiya  Sakata Yoichi
Institution:Division of Cell and Molecular Medicine, The Center for Molecular Medicine, Jichi Medical School, Tochigi-ken 329-0498, Japan.
Abstract:
Keywords:hemophilia  gene therapy  simian immunodeficiency virus  hematopoietic stem cell
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