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The Protective Effects of Levetiracetam on a Human iPSCs-Derived Spinal Muscular Atrophy Model
Authors:Ando  Shiori  Funato  Michinori  Ohuchi  Kazuki  Inagaki  Satoshi  Sato  Arisu  Seki  Junko  Kawase  Chizuru  Saito  Toshio  Nishio  Hisahide  Nakamura  Shinsuke  Shimazawa  Masamitsu  Kaneko  Hideo  Hara  Hideaki
Institution:1.Molecular Pharmacology, Department of Biofunctional Evaluation, Gifu Pharmaceutical University, 1-25-4 Daigaku-nishi, Gifu, 501-1196, Japan
;2.Department of Clinical Research, National Hospital Organization, Nagara Medical Center, Gifu, Japan
;3.Division of Child Neurology, Department of Neurology, National Hospital Organization, Toneyama National Hospital, Toyonaka, Osaka, Japan
;4.Department of Occupational Therapy, Faculty of Rehabilitation, Kobe Gakuin University, Kobe, Hyogo, Japan
;
Abstract:Neurochemical Research - Spinal muscular atrophy (SMA) is an inherited disease characterized by progressive motor neuron death and subsequent muscle weakness and is caused by deletion or mutation...
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